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An in vitro transcription plasmid for PKU gene therapy

Engineering a plasmid for PKU gene therapy, using RNA sequencing and bioinformatics to optimize RNA expression and evaluate the vector.

When
May 2022 – Sep 2023
Role
Student Researcher
Lab
Altuntaş Lab, Gene Editing
Institution
North American University (NAU)
Topics
  • Gene therapy
  • Phenylketonuria (PKU)
Methods
  • In vitro transcription
  • RNA sequencing
  • Bioinformatics

Engineered an in vitro transcription plasmid for PKU gene therapy, leveraging RNA sequencing and bioinformatics analysis to optimize RNA expression and evaluate vector efficacy.

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